Historic Breakthrough: Baby Cured of Genetic Disease While Still in the Womb
In an unprecedented medical breakthrough, doctors have successfully treated a fetus with spinal muscular atrophy (SMA) before birth, marking the first documented case of a baby being cured of a genetic disease in utero. The child, now almost three years old, shows no signs of SMA type 1, the most severe form of the disorder, which is often fatal in infancy. This revolutionary treatment could reshape the future of prenatal genetic medicine and open doors for treating other congenital conditions before birth.
What Is Spinal Muscular Atrophy (SMA)?
SMA is a devastating genetic disease that affects motor neurons, the nerve cells responsible for muscle movement. It is caused by a mutation in the SMN1 gene, which is essential for producing the survival motor neuron (SMN) protein. Without eno...